Speakers

Paolo Martini

CSO

Moderna Therapeutics

Klaus Gregorius

Co-Founder & CSO

MipSalus

Chris Carpenter

CMO

Rubius Therapeutics

David Pauza

Chief Scientific Officer

American Gene Technologies

Katherine Cygnar

Senior Staff Scientist

Regeneron

Deya Corzo

CMO

Sigilon Therapeutics

Dustin Armstrong

CSO

Valerion Therapeutics

Sonia Poli

CSO

Minoryx

Mathias Schmidt

CEO

ArmaGen

Neil Smith

VP, Research and Development

Censa Pharmaceuticals

Art Taveras

CSO

Comet Therapeutics

Lex Cowsert

Director of Research

National PKU Alliance

Paul Humphrey

Director Patient Advocacy

BioMarin

Reena Kartha

Associate Director Translational Pharmacology, Center for Orphan Drug Research

University of Minnesota

Christeen Moburg

Director Patient Advocacy

Sangamo Therapeutics

Michael Blum

Vice President, Commercial Strategy

Homology Medicines

Adith Venkiteshwaran

Global New Product Planning, Rare Diseases

Sanofi

Marcia Sellos-Moura

Senior VP

Orphan Technologies

Sue Khan

Executive Director

NTSAD

Frank Glavin

CEO

Orphan Technologies

Paul Orchard

Professor Pediatric Blood & Marrow Transplantation

University of Minnesota

Sophie Olivier

CSO

Lysogene

Fatemeh (Mitra) Tavakkoli

Clinical Development Lead

Spark Therapeutics

Jason Mallory

Clinical Development Lead

Spark Therapeutics