Speakers Paolo Martini CSO Moderna Therapeutics David Pauza Chief Scientific Officer American Gene Technologies Katherine Cygnar Senior Staff Scientist Regeneron Sonia Poli Development & Strategy Advisor Minoryx Mathias Schmidt CEO ArmaGen Art Taveras CSO Comet Therapeutics Asif Paker VP Clinical Development SwanBio Therapeutics Alfica Sehgal VP, Head of Discovery Camp4 Therapeutics Reena Kartha Associate Director Translational Pharmacology, Center for Orphan Drug Research University of Minnesota Christeen Moburg Director Patient Advocacy Sangamo Therapeutics Paul Orchard Professor Pediatric Blood & Marrow Transplantation University of Minnesota Sophie Olivier CSO Lysogene Kevin Fowler President The Voice of the Patient Inc Jodie Gillon VP Patient Advocacy & Clinical Affairs Abeona Therapeutics Joslyn Crowe Executive Director National Niemann Pick Disease Foundation Joseph Musumeci President BluePrint Orphan